The blood-brain barrier stands as one of evolution's most sophisticated achievements. After 111 years of failed attempts, two companies join to try to crack human biology's finest safe. Will they succeed, providing hope for millions of people living with neurodegenerative diseases?

In early 2025, a baby named KJ became the first person ever treated with a fully personalized CRISPR gene-editing therapy. Born with a rare, life-threatening disorder, KJ’s story is more than a medical miracle, it is a glimpse into a new era where cures for rare diseases could become reality for many more children.

Dive into the article to learn how that happened, with insights into the science and the ripples this case has had in the world of gene editing!